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       #Post#: 1111--------------------------------------------------
       FDA expedites review of ocrelizumab for treating PPMS
       By: agate Date: February 17, 2016, 6:57 pm
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       From the MSAA, February 17, 2016:
       [quote]
       FDA Expedites Review of Ocrelizumab for the Treatment of PPMS
       The United States Food and Drug Administration (FDA) has granted
       “Breakthrough Therapy Designation” for ocrelizumab, an
       experimental medication presently under investigation for the
       treatment of primary-progressive multiple sclerosis (PPMS). At
       this time, no treatments are available for this less-common form
       of MS.
       With this designation, the FDA affirms: (1) the medication would
       be used to treat a serious condition; (2) preliminary clinical
       evidence indicates that the drug may demonstrate substantial
       improvement over existing therapies; and (3) the review process
       would be expedited to within 60 days.
       In contrast to relapsing-remitting MS (RRMS) – the most-common
       type of multiple sclerosis affecting 80 to 85 percent of people
       diagnosed with MS – about 10 percent of the MS population is
       diagnosed with PPMS.
       Individuals with PPMS experience a steady worsening of symptoms
       from the start, without the periodic relapses and remissions
       experienced by people with RRMS. While 13 disease-modifying
       therapies are currently approved for relapsing forms of MS, no
       long-term treatments have been approved for PPMS.
       Genentech, a member of the Roche group, is the company
       developing ocrelizumab. They have submitted the brand name
       Ocrevus™ to the FDA for this investigational medication, noting
       that this is the first drug for MS that has been designated as
       breakthrough therapy by the FDA.
       Ocrelizumab is an investigational, humanized monoclonal antibody
       designed to selectively target CD20-positive B cells. Genentech
       explains that these are a specific type of immune cell thought
       to be a key contributor to myelin and axonal damage, which can
       result in disability in people with MS.
       According to Genentech, the breakthrough designation is based on
       positive results from the pivotal Phase III ORATORIO study.
       Top-line results from this study were presented at the 31st
       congress of the European Committee for Treatment and Research in
       Multiple Sclerosis (ECTRIMS) in October 2015.
       These results stated that the trial met its primary endpoint,
       showing that treatment with ocrelizumab in PPMS significantly
       reduced the progression of clinical disability sustained for at
       least 12 weeks compared with placebo. Walking speed, as measured
       by the timed 25-foot walk, was improved by 29 percent. The
       incidence of adverse events associated with ocrelizumab was
       similar to placebo; the most common adverse events were
       mild-to-moderate infusion-related reactions. MRI hyper-intense
       T2 lesions were actually reduced by ocrelizumab, and
       brain-volume loss as viewed on MRI was reduced by 17.5 percent.
       ...
       Readers should note that this breakthrough designation with the
       expedited review period has only been granted by the FDA for the
       one indication, which is for the long-term treatment of PPMS.
       Genentech also plans to seek approval of the medication for the
       long-term treatment of relapsing forms of MS in the near future.
       They plan to submit data from additional Phase III studies to
       the FDA in the first half of 2016.
       MSAA Chief Medical Officer Dr. Jack Burks states, "This is very
       exciting news. Ocrelizumab is the first disease-modifying
       therapy with positive disability results in PPMS. In addition,
       the safety data were similar to placebo controls. However, FDA
       approval will require intense scrutiny of these data.
       Effectiveness combined with safety is the magic formula, and
       we’ll see if the FDA agrees that ocrelizumab meets both
       requirements for approval in PPMS."
       For more information or to speak with a trained Client Services
       Specialist, please call MSAA's Helpline at (800) 532-7667,
       extension 154. Questions to MSAA's Client Services department
       may also be emailed to MSquestions@mymsaa.org.
       ________
       Written by Susan Wells Courtney, MSAA Senior Writer
       Reviewed by Jack Burks, MD, MSAA Chief Medical Officer[/quote]
       #Post#: 1265--------------------------------------------------
       Re: FDA expedites review of ocrelizumab for treating PPMS
       By: agate Date: June 24, 2016, 1:35 pm
       ---------------------------------------------------------
       From the International Progressive MS Alliance, which had its
       Second Scientific Congress in May:
       [quote]Federal Drug Administration designates experimental
       therapy, ocrelizumab as ‘Breakthrough Therapy’ for treatment of
       primary-progressive MS
       Genentech, a member of the Roche Group, announced in a February
       16 press release that the experimental therapy ocrelizumab has
       been granted ‘Breakthrough Therapy designation’ by the U.S. Food
       and Drug Administration (FDA) for the treatment of people with
       primary-progressive MS.  This designation means that once
       Genentech files for approval of ocrelizumab to treat
       primary-progressive MS, the review process can be expedited.
       According to the release, Genentech plans to pursue marketing
       approval for both primary-progressive MS and relapsing multiple
       sclerosis, and will submit data from three phase III studies to
       the FDA in the first half of 2016.
       Breakthrough Therapy designation can expedite the development
       and review of therapies intended to treat a serious condition
       when clinical evidence indicates that the treatment may
       demonstrate substantial improvement over available therapy.  The
       designation was granted to ocrelizumab based on phase III trial
       results presented at the European Committee for Treatment and
       Research in MS in late 2015.  Compared to placebo, ocrelizumab
       significantly reduced the risk of progression of clinical
       disability by 24% in 732 people with primary-progressive MS.
       Read more about these results.
       “An effective treatment for people with progressive MS would be
       truly life-changing,” said Dr. Alan Thompson, chair of the
       International Progressive MS Alliance Scientific Steering
       Committee. “We await the detailed safety and efficacy data with
       great anticipation, and thanks to this expedited review process
       we are very much looking forward to hearing of ocrelizumab’s
       future developments and implications.”
       
       --Read more on the ‘Breakthrough Therapy designation’ at the FDA
       website, and more on ocrelizumab at the National MS Society
       (NMSS) website.
       - See more at:
  HTML http://www.progressivemsalliance.org/announcements/federal-drug-administration-designates-experimental-therapy-ocrelizumab-as-breakthrough-therapy-for-treatment-of-primary-progressive-ms/#sthash.MI117MgB.dpuf
  HTML http://www.progressivemsalliance.org/announcements/federal-drug-administration-designates-experimental-therapy-ocrelizumab-as-breakthrough-therapy-for-treatment-of-primary-progressive-ms/#sthash.MI117MgB.dpuf[/quote]
       #Post#: 1266--------------------------------------------------
       Re: FDA expedites review of ocrelizumab for treating PPMS
       By: agate Date: June 24, 2016, 1:39 pm
       ---------------------------------------------------------
       Phase 2 and 3 trials of ocrelizumab are summarized here:
       [quote]Relapsing remitting MS
       Two phase 3 trials (OPERA I and OPERA II) were completed in June
       2015 and Roche reported positive outcomes for the effectiveness
       of ocrelizumab as a treatment for relapsing remitting MS against
       interferon beta-1a (also known as Rebif). The trials involved
       over 1,600 people and after two years, the study is reported to
       show that ocrelizumab reduced the annual relapse rate by 46% in
       OPERA 1, 47% in OPERA II and the progression of clinical
       disability by 40%, as measured by the Expanded Disability Status
       Scale (EDSS). Additionally, the study has been reported to show
       that ocrelizumab reduced the number of lesions in the brain, as
       measured by MRI scans by 94%.
       Roche have also reported at a conference in April 2016 that
       around 50% of people taking ocrelizumab saw no evidence of
       disease activity (NEDA) in both OPERA I and OPERA II, this was
       compared to 25-30% of people taking interferon-beta-1a. NEDA is
       defined as no relapses, no confirmed disability progression as
       measured by EDSS, and no new or enlarging lesions.
       Primary Progressive MS
       A phase 3 trial (ORATORIO) began in 2011 to test ocrelizumab
       against placebo in 732 people with primary progressive MS. This
       involved two infusions 14 days apart in each treatment cycle.
       Top-line results announced by Roche at a conference in April
       2016 show treatment with ocrelizumab led to a reduction in the
       progression of clinical disability by 25% compared to placebo.
       This reduction was sustained for at least 24 weeks and was
       measured by the Expanded Disability Status Scale (EDSS). Roche
       also reported that ocrelizumab reduced the rate of brain atrophy
       (shrinkage) by 17.5%.[/quote]
       From the UK MS Society Website at
  HTML https://www.mssociety.org.uk/ms-research/treatments-in-the-pipeline/ocrelizumab
  HTML https://www.mssociety.org.uk/ms-research/treatments-in-the-pipeline/ocrelizumab.
       #Post#: 1281--------------------------------------------------
       MSAA announces availability of ocrelizumab for some PPMS patient
       s soon
       By: agate Date: July 6, 2016, 2:44 pm
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       According to this message from the MS Association of America,
       ocrelizumab should soon be available at some centers (not chosen
       yet) for people diagnosed with PPMS, between the ages of 18 and
       55, and with an EDSS score between 2.0 and 6.5:
  HTML http://mymsaa.org/news/experimental-medication-ppms/
  HTML http://mymsaa.org/news/experimental-medication-ppms/
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